Market DemandPatients are willing to abandon established therapies to access a potential permanent solution, showing strong commercial demand for Intellia’s treatment.
Product EfficacyNex-z could transform the ATTR-PN treatment paradigm with its best-in-disease efficacy potential.
Research And DevelopmentIntellia has fully enrolled ~60 patients in the pivotal Phase 3 trial of lonvo-z just nine months after first dosing, indicating strong demand for the one-time gene-editing treatment.