Clinical DevelopmentThe completed enrollment of the low dose cohort in RP-A601's Ph1 trial for PKP2-ACM is a significant development, with initial data expected soon.
Financial PositionRCKT ended with $372.3M in cash, which is expected to be sufficient into 3Q26.
Market OpportunityRP-A601 for Plakophilin-2 Related Arrhythmogenic Cardiomyopathy could confer a larger commercial opportunity, despite not being clinically derisked yet.
Therapeutic PotentialRCKT's therapies likely offer a life-long effect as they target the heart, unlike most liver-targeted gene therapies with limited durability.