Clinical Trial SuccessCRISPR Therapeutics presented preliminary safety and efficacy data from the trial of their 2nd-gen allo CD19 CAR-T therapy CTX112 showing a 67% overall response rate and 50% complete response rate.
Financial PositionCRISPR Therapeutics maintains a strong cash position, which is advantageous in conditions of market uncertainty.
Regulatory Approvals And PartnershipsVertex recently negotiated a voluntary agreement with the Centers for Medicare & Medicaid Services, providing a single outcomes-based arrangement for Casgevy to ensure broad and equitable access.