Clinical Trial AdvancementsBEAM-302 advances toward pivotal readiness as the first, one-time, in vivo program to directly correct a disease-causing mutation in AATD, with favorable safety profile and promising clinical results.
Collaborations And PartnershipsThe collaboration with Bristol Myers Squibb, which involves a $1.5 billion acquisition of Beam's collaborator Orbital Therapeutics, further validates Beam's technology leadership in mRNA and targeted lipid nanoparticle delivery.
Regulatory EnvironmentBeam stands out as a clear beneficiary of the FDA’s draft guidances, which signal a more enabling regulatory environment for next-generation gene editing technologies.