Financial PerformanceProbability adjusted peak sales increases to approximately $3BN, raising the PT to $35 from $25, reiterating the BUY rating.
Program AdvancementsBEAM has showcased its ability to generate the best-in-class profile in a disease with well characterized underlying disease drivers.
Regulatory EnvironmentBeam stands out as a clear beneficiary of the FDA’s draft guidances, which signal a more enabling regulatory environment for next-generation gene editing technologies.