Clinical DevelopmentThe transition of clinical sites to FREEDOM2-DM1, a Phase 2 multiple ascending dose study, accelerates the clinical timeline and potentially saves 3-6 months.
Efficacy And SafetyThe safety profile supports the value of PepGen’s EDO platform, with no adverse effects seen in kidney biomarkers or electrolyte levels.
Market PotentialIf splicing correction continues to correlate with clinical improvement, the program could attract acquisition interest due to the growing industry focus on DM1.