Clinical Study ResultsNfL levels did not show a decrease or trend in reduction in this study, but a longer-term study might be able to demonstrate an impact in the NfL levels especially if the caudate data holds true.
Market Position'N531 addresses only a fraction of patients, making the commercial outlook less clear especially against established players like SRPT.
Patient OutcomesThere is a trend of increase in NfL levels over time, with some patients showing higher-than-placebo levels, which might cap near-term upside.