Financial StabilityManagement's recent financing extended DYN's runway into 3Q27, enabling derisking of the DM1 program and commercialization of the DMD program.
Regulatory SupportThe FDA granted Breakthrough Therapy Designation to DYNE-251 for the treatment of patients with Duchenne muscular dystrophy, highlighting unmet need and FDA support.
Therapeutic EfficacyDYNE-251 delivered robust muscle content-adjusted dystrophin expression and sustained effect on functional outcomes, which can enable BLA submission for accelerated approval.