Clinical Efficacy And BiomarkerRegistrational expansion cohort data demonstrated robust dystrophin production alongside consistent functional improvements across multiple measures, supporting meaningful clinical benefit for exon 51 Duchenne patients.
Regulatory PathwayManagement confirmed a regulatory filing is on track for 2Q26 to pursue accelerated approval, creating a clear near-term regulatory catalyst for the program.
Strategic Validation And M&A InterestNovartis's acquisition of Avidity validated TfR1-mediated RNA delivery approaches and increased strategic interest in the FORCE platform, enhancing Dyne's appeal as a potential M&A target.