Market PotentialSMA is a sizable $4-5B established commercial market where SRRK could capture at least $1-2B.
Regulatory MilestonesThe FDA has granted apitegromab Fast Track, Orphan Drug, and Rare Pediatric Disease designations.
Research And DevelopmentScholar Rock's research platform could enable selective targeting of TGF-β proteins, with apitegromab potentially being the first effective and safe myostatin inhibitor.