Funding StrategyRARE strengthened liquidity with $400M non-dilutive financing from OMERS, deferring payments until 2028 to support launch readiness and maintain its path to profitability in 2027.
Market OpportunityThe OI market opportunity is estimated to be 50-100% larger than XLH, with pricing expected to mirror Crysvita and early uptake likely in severe Type 3/4 patients.
Therapeutic AdvancesThe results from the Phase 3 GlucoGene study with DTX401 showed greater reductions in daily cornstarch intake and maintained low levels of hypoglycemia, indicating strong therapeutic benefits.