Clinical DevelopmentThe pivotal ORBIT study of setrusumab in osteogenesis imperfecta is proceeding to the second interim analysis, highlighting ongoing clinical advancement.
Financial PerformanceUltragenyx reported preliminary 2024 total revenues of $555-560M, exceeding the consensus of $536M.
Regulatory ProgressUltragenyx submitted the Biologics License Application for UX111, demonstrating forward progress in their gene therapy development.