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BioMarin Pharmaceutical (BMRN)
NASDAQ:BMRN
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BioMarin Pharmaceutical (BMRN) Price & Analysis

2,403 Followers

BMRN Stock Chart & Stats

$54.64
$0.93(1.37%)
At close: 4:00 PM EST
$54.64
$0.93(1.37%)

Bulls Say, Bears Say

Bulls Say
Acquisition Strengthens PortfolioPlanned acquisition of Amicus expands the enzyme replacement therapy portfolio and reduces competitive exposure for the Voxzogo franchise, supporting a more diversified growth profile.
Clinical Efficacy In Very Young PatientsNew trial data showed statistically significant and sustained improvement in body proportionality for achondroplasia patients who began treatment at a very young age, supporting stronger clinical positioning for earlier intervention.
Market Adoption UpsideLow current penetration among eligible achondroplasia patients indicates substantial runway to increase Voxzogo adoption and expand revenue as more patients start therapy.
Bears Say
Emerging Competitive Pressure From Weekly Injectables And Oral AgentsApproval and advancement of once-weekly injectables and emerging oral FGFR competitors pose layered competitive threats that could erode Voxzogo market share over time.
International Regulatory DependenceHeavy reliance on markets outside the United States makes Voxzogo vulnerable to unfavorable regulatory decisions in Europe, which could materially affect international sales.
Safety Concerns From Slipped Capital Femoral EpiphysisReports of slipped capital femoral epiphysis in investigator-led studies led to discontinuation of several programs and raise safety uncertainty for broader use of the drug.

BioMarin Pharmaceutical News

BMRN FAQ

What was BioMarin Pharmaceutical’s price range in the past 12 months?
BioMarin Pharmaceutical lowest stock price was $50.76 and its highest was $66.28 in the past 12 months.
    What is BioMarin Pharmaceutical’s market cap?
    BioMarin Pharmaceutical’s market cap is $10.40B.
      When is BioMarin Pharmaceutical’s upcoming earnings report date?
      BioMarin Pharmaceutical’s upcoming earnings report date is Aug 04, 2026 which is in 91 days.
        How were BioMarin Pharmaceutical’s earnings last quarter?
        BioMarin Pharmaceutical released its earnings results on May 04, 2026. The company reported $0.54 earnings per share for the quarter, missing the consensus estimate of $0.694 by -$0.154.
          Is BioMarin Pharmaceutical overvalued?
          According to Wall Street analysts BioMarin Pharmaceutical’s price is currently Undervalued. Get more investment ideas with TipRanks Premium
            Does BioMarin Pharmaceutical pay dividends?
            BioMarin Pharmaceutical does not currently pay dividends.
            What is BioMarin Pharmaceutical’s EPS estimate?
            BioMarin Pharmaceutical’s EPS estimate is 0.9.
              How many shares outstanding does BioMarin Pharmaceutical have?
              BioMarin Pharmaceutical has 192,323,360 shares outstanding.
                What happened to BioMarin Pharmaceutical’s price movement after its last earnings report?
                BioMarin Pharmaceutical reported an EPS of $0.54 in its last earnings report, missing expectations of $0.694. Following the earnings report the stock price went down -0.477%.
                  Which hedge fund is a major shareholder of BioMarin Pharmaceutical?
                  Currently, no hedge funds are holding shares in BMRN
                  What is the TipRanks Smart Score and how is it calculated?
                  Smart Score combines eight research factors - such as analyst recommendations, hedge fund trends, and technical indicators - to measure a stock’s outlook. These signals are unified into a single score that reflects bullish or bearish momentum. See detailed methodology

                    Company Description

                    BioMarin Pharmaceutical

                    BioMarin Pharmaceutical Inc. develops and commercializes therapies for people with serious and life-threatening rare diseases and medical conditions. Its commercial products include Vimizim, an enzyme replacement therapy for the treatment of mucopolysaccharidosis (MPS) IV type A, a lysosomal storage disorder; Naglazyme, a recombinant form of N-acetylgalactosamine 4-sulfatase for patients with MPS VI; and Kuvan, a proprietary synthetic oral form of 6R-BH4 that is used to treat patients with phenylketonuria (PKU), an inherited metabolic disease. The company's commercial products also comprise Palynziq, a PEGylated recombinant phenylalanine ammonia lyase enzyme, which is delivered through subcutaneous injection to reduce blood Phe concentrations; Brineura, a recombinant human tripeptidyl peptidase 1 for the treatment of patients with ceroid lipofuscinosis type 2, a form of Batten disease; Voxzogo, a once daily injection analog of c-type natriuretic peptide for the treatment of achondroplasia; and Aldurazyme, a purified protein designed to be identical to a naturally occurring form of the human enzyme alpha-L-iduronidase. In addition, it develops valoctocogene roxaparvovec, an adeno associated virus vector, which is in Phase III clinical trial for the treatment of patients with severe hemophilia A; BMN 307, an AAV5 mediated gene therapy, which is in Phase 1/2 clinical trial to normalize blood Phe concentration levels in patients with PKU; and BMN 255 that is in Phase 1/2 clinical trial for treating primary hyperoxaluria. The company serves specialty pharmacies, hospitals, and non-U.S. government agencies, as well as distributors and pharmaceutical wholesalers in the United States, Europe, Latin America, and internationally. BioMarin Pharmaceutical Inc. has license and collaboration agreements with Sarepta Therapeutics, Ares Trading S.A., Catalyst Pharmaceutical Partners, Inc., and Asubio Pharma Co., Ltd. The company was incorporated in 1996 and is headquartered in San Rafael, California.

                    BioMarin Pharmaceutical (BMRN) Earnings & Revenues

                    BMRN Company Deck

                    BMRN Earnings Call

                    Q1 2026
                    0:00 / 0:00
                    Earnings Call Sentiment|Positive
                    The call conveyed a predominantly positive outlook driven by the recent Amicus acquisition, upgraded 2026 revenue guidance (~20% total revenue growth and ~30% Enzyme Therapies growth at midpoint), strong underlying patient demand (Voxzogo patients +20% y/y; Enzyme Therapies +6% y/y), and multiple near‑term clinical catalysts. Near‑term softness in reported Q1 revenue, a $31M one‑time manufacturing charge, higher operating expenses and modest 2026 EPS dilution are notable headwinds, but management attributes much of the revenue softness to order timing and positions acquisition dilution as temporary with accretion expected within 12 months and substantial accretion in 2027. Overall, the positives (deal, guidance lift, patient growth, pipeline milestones) outweigh the one‑time charges and timing issues.View all BMRN earnings summaries

                    BMRN Revenue Breakdown

                    28.98%28.98%19.42%17.37%12.56%21.66%
                    28.98% VIMIZIM
                    19.42% VOXZOGO
                    17.37% NAGLAZYME
                    12.56% PALYNZIQ
                    21.66% Other
                    tipranks

                    BMRN Stock 12 Month Forecast

                    Average Price Target

                    $93.07
                    ▲(70.33% Upside)
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34,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 7, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":54.86,"date":1759276800000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 46,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 10, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":53.57,"date":1761955200000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 27,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 8, \t&nbsp;</span>\n   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