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BioMarin Pharmaceutical (BMRN)
NASDAQ:BMRN

BioMarin Pharmaceutical (BMRN) Price & Analysis

2,391 Followers

BMRN Stock Chart & Stats

$54.53
$0.93(1.37%)
At close: 4:00 PM EST
$54.53
$0.93(1.37%)

Bulls Say, Bears Say

Bulls Say
Clinical EfficacyClinical trial data showed statistically significant and sustained improvements in body proportionality for achondroplasia patients who began Voxzogo treatment before age two, supporting earlier initiation and clinical differentiation.
Market Penetration UpsideLow current market penetration among eligible achondroplasia patients indicates substantial upside for Voxzogo adoption as awareness and access expand, which could drive revenue growth.
Portfolio DiversificationAcquisition of Amicus expands the enzyme replacement therapy portfolio and reduces exposure to competition for Voxzogo, providing diversification that could support valuation and debt reduction.
Bears Say
Competitive ConvenienceApproval of a once-weekly injectable rival offers a more convenient dosing option than Voxzogo's once-daily injection and could pressure U.S. market share.
Geographic Regulatory RiskHeavy reliance on international sales makes Voxzogo vulnerable to regulatory decisions in Europe, where approval of competing therapies could significantly weaken global revenues.
Safety ConcernsReports of slipped capital femoral epiphysis in investigator-led studies prompted discontinuation of several development programs, creating safety-related uncertainty that could constrain label expansion.

BioMarin Pharmaceutical News

BMRN FAQ

What was BioMarin Pharmaceutical’s price range in the past 12 months?
BioMarin Pharmaceutical lowest stock price was $50.76 and its highest was $66.28 in the past 12 months.
    What is BioMarin Pharmaceutical’s market cap?
    BioMarin Pharmaceutical’s market cap is $10.49B.
      When is BioMarin Pharmaceutical’s upcoming earnings report date?
      BioMarin Pharmaceutical’s upcoming earnings report date is Apr 29, 2026 which is in 15 days.
        How were BioMarin Pharmaceutical’s earnings last quarter?
        BioMarin Pharmaceutical released its earnings results on Feb 23, 2026. The company reported -$0.24 earnings per share for the quarter, missing the consensus estimate of $0.169 by -$0.409.
          Is BioMarin Pharmaceutical overvalued?
          According to Wall Street analysts BioMarin Pharmaceutical’s price is currently Undervalued. Get more investment ideas with TipRanks Premium
            Does BioMarin Pharmaceutical pay dividends?
            BioMarin Pharmaceutical does not currently pay dividends.
            What is BioMarin Pharmaceutical’s EPS estimate?
            BioMarin Pharmaceutical’s EPS estimate is 0.73.
              How many shares outstanding does BioMarin Pharmaceutical have?
              BioMarin Pharmaceutical has 192,323,360 shares outstanding.
                What happened to BioMarin Pharmaceutical’s price movement after its last earnings report?
                BioMarin Pharmaceutical reported an EPS of -$0.24 in its last earnings report, missing expectations of $0.169. Following the earnings report the stock price went down -0.477%.
                  Which hedge fund is a major shareholder of BioMarin Pharmaceutical?
                  Currently, no hedge funds are holding shares in BMRN
                  What is the TipRanks Smart Score and how is it calculated?
                  Smart Score combines eight research factors - such as analyst recommendations, hedge fund trends, and technical indicators - to measure a stock’s outlook. These signals are unified into a single score that reflects bullish or bearish momentum. See detailed methodology

                    Company Description

                    BioMarin Pharmaceutical

                    BioMarin Pharmaceutical Inc. develops and commercializes therapies for people with serious and life-threatening rare diseases and medical conditions. Its commercial products include Vimizim, an enzyme replacement therapy for the treatment of mucopolysaccharidosis (MPS) IV type A, a lysosomal storage disorder; Naglazyme, a recombinant form of N-acetylgalactosamine 4-sulfatase for patients with MPS VI; and Kuvan, a proprietary synthetic oral form of 6R-BH4 that is used to treat patients with phenylketonuria (PKU), an inherited metabolic disease. The company's commercial products also comprise Palynziq, a PEGylated recombinant phenylalanine ammonia lyase enzyme, which is delivered through subcutaneous injection to reduce blood Phe concentrations; Brineura, a recombinant human tripeptidyl peptidase 1 for the treatment of patients with ceroid lipofuscinosis type 2, a form of Batten disease; Voxzogo, a once daily injection analog of c-type natriuretic peptide for the treatment of achondroplasia; and Aldurazyme, a purified protein designed to be identical to a naturally occurring form of the human enzyme alpha-L-iduronidase. In addition, it develops valoctocogene roxaparvovec, an adeno associated virus vector, which is in Phase III clinical trial for the treatment of patients with severe hemophilia A; BMN 307, an AAV5 mediated gene therapy, which is in Phase 1/2 clinical trial to normalize blood Phe concentration levels in patients with PKU; and BMN 255 that is in Phase 1/2 clinical trial for treating primary hyperoxaluria. The company serves specialty pharmacies, hospitals, and non-U.S. government agencies, as well as distributors and pharmaceutical wholesalers in the United States, Europe, Latin America, and internationally. BioMarin Pharmaceutical Inc. has license and collaboration agreements with Sarepta Therapeutics, Ares Trading S.A., Catalyst Pharmaceutical Partners, Inc., and Asubio Pharma Co., Ltd. The company was incorporated in 1996 and is headquartered in San Rafael, California.

                    BioMarin Pharmaceutical (BMRN) Earnings & Revenues

                    BMRN Company Deck

                    BMRN Earnings Call

                    Q4 2026
                    0:00 / 0:00
                    Earnings Call Sentiment|Positive
                    The call conveyed a largely positive commercial and operational performance: record revenues, strong YOY growth for Voxzogo and enzyme therapies, improved profitability (non-GAAP EPS and operating cash flow), clear near-term R&D catalysts, and strategic acquisitions that should expand the portfolio and future revenues. Headwinds were acknowledged and quantified — notably the Roctavian withdrawal and related charges, one-time Q4 order timing effects leading to a weaker Q1, lower royalty expectations, routine market-access renegotiations in select countries, and modest near-term dilution and costs tied to the Amicus acquisition. Management provided concrete 2026 guidance (excluding Amicus post-close contributions) and explained assumptions for competitive scenarios. Overall, positives (robust growth, cash generation, pipeline catalysts, and strategic M&A) outweigh the defined near-term and one-time negatives.View all BMRN earnings summaries

                    BMRN Revenue Breakdown

                    28.98%28.98%19.42%17.37%12.56%21.66%
                    28.98% VIMIZIM
                    19.42% VOXZOGO
                    17.37% NAGLAZYME
                    12.56% PALYNZIQ
                    21.66% Other
                    tipranks

                    BMRN Stock 12 Month Forecast

                    Average Price Target

                    $91.14
                    ▲(67.14% Upside)
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67,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 5, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":59.09,"date":1756684800000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 73,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 7, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":54.86,"date":1759276800000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 81,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 11, \t&nbsp;</span>\n   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