Financial PositionEnded 2Q24 with approximately $524M in cash, which uniQure expects, together with the estimated savings from the restructuring measures, should fund operations through the end of.
Gene Therapy ProgramsMultiple gene therapy pipeline programs advancing in Phase 1/2.
Regulatory ProgressQURE was granted the RMAT designation in June that allows sponsors to have early and frequent interactions with the FDA, enabling increased collaboration and the opportunity for expedited product development.