Drug Designation And Pricing PotentialBoth relutrigine and elsunersen have Orphan Drug Designation and Rare Pediatric Disease Designation with the FDA, with promising results in studies and premium pricing potential.
Enrollment And Program CommitmentPRAX has raised its total projected enrollment to 1,000 participants, indicating a strong commitment to its Essential Tremor program.
Market Entry And ValuationAt a market cap of less than $900 million, PRAX's valuation is attractive with multiple opportunities that could collectively drive over $4 billion in peak sales.
Trial Results And Market PotentialTopline results from PRAX's Phase 3 trials for ulixacaltamide in Essential Tremor are expected to potentially trigger significant upside, as the condition affects around 7 million US patients in need of better treatment options.