Efficacy And SafetyPositive data from the open-label study showed impressive efficacy results for nomlabofusp in Friedreich's Ataxia.
Regulatory ProgressNomlabofusp is part of the FDA START program with regular agency interactions, boosting investor confidence.
Therapy AdvancementsMeaningful advancements in Larimar’s frataxin replacement therapy program, nomlabofusp, for Friedreich’s ataxia were observed, showing promising disease-modifying potential.