Efficacy And ImprovementFunctional improvement from baseline on clinical endpoints was observed with nomlabofusp treatment out to one year, which is divergent from FA-COMS natural history and has not been observed before in an FA interventional trial.
Regulatory InteractionNomlabofusp is part of the FDA START program, and the company is having regular agency interactions, which could provide investor confidence.
Therapy AdvancementsThis quarter saw meaningful advancements in Larimar’s frataxin replacement therapy program, nomlabofusp (nomla), for Friedreich’s ataxia (FA).