Clinical DevelopmentDISC-0974 demonstrated clinically meaningful and sustained increases in hemoglobin that surpass those reported by competitors.
Market PotentialFocus remains on bito for its orphan indication with limited competition and blockbuster potential, with active engagement with EU regulators and preparation for commercial launch.
Regulatory ProgressFor bitopertin, near-term focus remains centered on a regulatory update that is expected to confirm an accelerated approval pathway in erythropoietic protoporphyria.