Clinical EfficacyPrevious studies have shown significant improvements in sunlight tolerance for patients using bitopertin, indicating strong treatment efficacy.
Market PotentialEPP is a pan ethnic disorder with an estimated ~20k patients in the U.S., indicating a significant potential market for effective treatments.
Regulatory ApprovalThe FDA announced that bitopertin has been selected as one of the first nine recipients of the Commissioner’s National Priority Review Voucher for the treatment of erythropoietic protoporphyria, accelerating the drug application review timelines to 1-2 months.