Financial OutlookBitopertin could be a significant drug with orphan indication and limited competition, potentially reaching a value of $600 million by 2030 with blockbuster potential.
Market PotentialBitopertin is likely to reach the market faster and with a higher probability, potentially becoming the first disease-modifying agent with a clear and direct mechanism of action for its condition.
Regulatory ApprovalPositive feedback from an End-of-Phase 2 meeting with FDA could allow for a substantially accelerated path to market for lead asset bitopertin in erythropoietic protoporphyria.