European Market ExpansionZevra filed a marketing authorization application with the European Medicines Agency for arimoclomol, marketed in the U.S. as Miplyffa, for the treatment of Niemann-Pick disease type C (NPC).
FDA ApprovalZevra received FDA approval of Miplyffa in combination with miglustat for the treatment of neurological manifestations of Niemann-Pick disease type C (NPC).
Product Launch And Revenue GrowthMiplyffa continues to show strong early uptake, generating revenue of $21.5M and 129 patient enrollments in total.