Clinical Trial ProgressPhase 2a trial for '719 as an add-on to standard care in CF patients has been initiated, with data expected in mid-2026, indicating progress in clinical trials.
Financial StabilitySION has $325 million in cash, providing operational funding through 2028, ensuring financial stability for future developments.
Therapeutic PotentialNew preclinical data suggests '719 and '451 can restore F508del-CFTR half-life to normal levels, indicating strong therapeutic potential.