Clinical Trial OutcomesPhase 3 SELVA trial met primary and pre‑specified secondary endpoints with statistically significant and clinically meaningful improvements, indicating strong efficacy for QTORIN rapamycin in microcystic lymphatic malformations.
Commercial PotentialPhysician surveys and key opinion leader feedback indicate likely frontline adoption and meaningful patient uptake, while experienced commercial hires and platform expansion plans support a scalable launch into additional mTOR‑driven indications.
Safety ProfileSafety results showed mostly mild application‑site effects, low systemic drug levels, and strong patient continuation into extension studies, supporting tolerability for chronic use.