Clinical EfficacyNGN-401 is delivering deep, multi-domain, durable gains with zero regression, with patients exceeding pivotal responder bar.
Financial StabilityNeurogene has a cash runway sufficient to fund operations into the first quarter of 2028, providing financial stability.
Regulatory AdvancementsNGN-401 was selected by the FDA for its START Pilot Program and has received multiple designations including RMAT, ODD, Fast Track, and RPDD.