Clinical Trial SuccessThe Phase 1 study enrolled 72 healthy volunteers, males and females, up to the age of 64 years, confirming that single and multiple doses of GT-02287 were safe and generally well tolerated up to and including the highest planned dose levels across all age groups.
Financial StabilityGain Therapeutics ended 2Q24 with $16.9M in cash and cash equivalents, following the completion of an equity offering that yielded roughly $10M in net proceeds.
Target Engagement AchievementThe favorable safety and tolerability profile at oral dose levels that resulted in therapeutic plasma levels, CNS exposure, and target engagement further strengthens GT-02287’s potential to be a lead treatment for Parkinson’s disease (PD).