Clinical Trial SuccessThe Phase 3 DRAGON trial of tinlarebant in adolescent Stargardt disease met the primary efficacy endpoint and demonstrated a significant reduction in the growth rate of retinal lesions compared with placebo.
Financial PositionBelite has raised $350M in a public offering, combined with existing cash, providing a strong financial position to advance commercialization efforts.
Regulatory ProgressTinlarebant has been granted Breakthrough Therapy, Fast Track, Rare Pediatric Disease, and Orphan Drug designations in the U.S., which should warrant accelerated approval in all territories.