Positive Results from STAAR Study in Fabry Disease
The registrational Phase 1/2 STAAR study showed positive top-line results with a mean annualized eGFR slope of almost 2 at 52 weeks across 32 patients. The FDA agreed that this metric will serve as the primary basis of approval under the accelerated approval pathway.
Neurology Genomic Medicine Company Milestone
Sangamo initiated its first clinical site in the Phase 1/2 STAND study in chronic neuropathic pain, marking its transition to a clinical stage neurology genomic medicine company.
Prion Disease Program Advances
A productive meeting with the U.K.'s MHRA was held for the preclinical prion disease program, with a planned CTA submission as early as mid-2026.
Equity Offering Completed
Sangamo completed an equity offering expected to fund planned operations into the fourth quarter of 2025, bridging to an anticipated Fabry commercialization agreement.