Clinical Trial ProgressEncouraging clinical activity and a manageable safety profile were demonstrated for OPGx-LCA5, with improvements in visual acuity reported in 5 out of 6 patients.
FDA SupportOpus Genetics plans on advancing to a pivotal study for OPGx-LCA5, having gained agreement with the FDA.
Gene Therapy AdvancementsOpus Genetics seeks to address Inherited Retinal Diseases (IRD) with gene therapy, with a focus on its lead gene therapy program, OPGx-LCA5, for which there are currently no treatment options and a high unmet need.