Clinical EfficacyPhase II data showed large, clinically meaningful reductions in absence and major motor seizures on objective brainwave measurements in patients who had failed multiple prior therapies, indicating strong potential for meaningful clinical benefit.
Pipeline Expansion And DevelopmentPlanned registrational pivotal trials alongside studies targeting Prader-Willi syndrome could validate the platform across rare epilepsies and genetic obesity, expanding the drug's clinical and commercial opportunity.
Safety And TolerabilityTrial results reported favorable tolerability with no drug-related serious adverse events and an absence of drowsiness that limits many existing anti-epileptic treatments, supporting potential for long-term use.