Clinical Data VariabilityObserved variability in CMP-001 ureagenesis results weakens confidence in consistent pharmacodynamic proof that regRNA targeting delivers anticipated biological effects.
Milestone-dependent Revenue RiskSignificant reliance on upfront, milestone and royalty payments from partnerships creates binary value drivers and limits predictable near-term revenue visibility.
Share Dilution And Market ReactionA discounted private placement pressured the share price and raised investor concerns about dilution and near-term selling pressure.