Promising Clinical Data in Fabry Disease
Presented detailed clinical data from the registrational STAAR study in Fabry disease, demonstrating the potential for ST-920 as a onetime durable treatment. The FDA reaffirmed the use of eGFR slope as an endpoint to support an accelerated approval pathway.
Advancement in Neurology Pipeline
Commenced patient enrollment in the Phase I/II STAND study for chronic neuropathic pain with ST-503. Also, progressed the prion program towards an anticipated CTA submission in mid-2026.
Extended Cash Runway
Received $6 million from Pfizer's exercise of a buyout option and continued business development discussions. Cash and cash equivalents are expected to fund operations into the first quarter of 2026.
Encouraging Preclinical Data
Presented updated nonclinical data demonstrating durability, potency, and selectivity of ST-503 in nonhuman primates and favorable safety profile.
FDA Endorsement
Received FDA's endorsement on clinical and CMC pathways for Fabry disease, which positively impacts business development discussions.