Strong Financial Performance
Net income per share was $3.12, up from $0.40 in 2023, marking the sixth straight quarter of positive EPS and the fourth consecutive quarter of sequential earnings growth.
Successful Launch of VYJUVEK
VYJUVEK U.S. launch continues to track in the top tier of rare disease launches with $341 million in net revenue within 18 months of launch and sequential revenue growth for six straight quarters.
Reimbursement Approvals Milestone
The company crossed 500 reimbursement approvals nationwide, with more than 510 patients approved as of February, indicating strong demand and market penetration.
Expanded Global Market Plans
Plans for VYJUVEK launch in Europe and Japan with anticipated regulatory approvals, targeting over 1,000 identified DEB patients in Germany and France alone.
Robust Pipeline Developments
Progress in gene delivery programs for cystic fibrosis, alpha-1 antitrypsin deficiency, and non-small cell lung cancer, with strong early signs of efficacy and validation of the lung as a second target tissue.