Clinical TrialsPositive interim results for the phase 1b ENERGY-1 trial in infants add to confidence in a positive pivotal readout.
Market OpportunityThere is encouragement by the market opportunity for INZ-701, given no approved therapies and prior data supporting its potential clinical benefit.
Regulatory DesignationsINZ-701 has orphan drug designation from the EMA and the FDA for the treatment of ENPP1 Deficiency, as well as FDA Fast Track designation and rare pediatric disease designation.