Zevra Therapeutics announces publication on arimoclomol

Zevra Therapeutics (ZVRA) announces the publication of “Mechanistic insights into arimoclomol mediated effects on lysosomal function in Niemann-pick type C disease” in Molecular Genetics and Metabolism. “This elucidation of MIPLYFFA’s highly differentiated mechanism of action marks a critical step in understanding its interactions with Niemann-Pick disease type C at a cellular level,” said Adrian Quartel, MD, FFPM, Zevra’s Chief Medical Officer. “These insights further confirm that MIPLYFFA addresses the underlying pathology of NPC and supports the long-term treatment benefit observed in our clinical trials. Our findings may inform more effective treatment strategies for patients.”