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Pharming Group’s Joenja® Receives NICE Recommendation for APDS Treatment

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Pharming Group ( (PHAR) ) has shared an announcement.

On April 23, 2025, Pharming Group N.V. announced that the National Institute for Health and Care Excellence (NICE) has recommended Joenja® (leniolisib) for reimbursement within the NHS in England and Wales. Joenja® is the first targeted treatment for activated phosphoinositide 3-kinase delta (PI3Kδ) syndrome (APDS), a rare primary immunodeficiency, and is available for patients aged 12 and older. This recommendation is based on positive results from a Phase III clinical trial, highlighting significant improvements in immune deficiency and dysregulation. The decision marks a significant milestone for Pharming, reinforcing its commitment to providing innovative treatments for rare diseases and improving the quality of life for patients with APDS.

Spark’s Take on PHAR Stock

According to Spark, TipRanks’ AI Analyst, PHAR is a Neutral.

Pharming Group’s stock score is driven by strengths in revenue growth and strategic initiatives highlighted in the earnings call. However, challenges in profitability, cash flow management, and a negative P/E ratio weigh on the score. Technical indicators suggest a neutral to bearish trend, indicating caution. Overall, the company shows potential for growth but must address financial inefficiencies to enhance stock performance.

To see Spark’s full report on PHAR stock, click here.

More about Pharming Group

Pharming Group N.V. is a global biopharmaceutical company focused on developing and commercializing innovative medicines for rare, debilitating, and life-threatening diseases. Headquartered in Leiden, the Netherlands, Pharming operates in over 30 markets across North America, Europe, the Middle East, Africa, and Asia-Pacific, offering a portfolio that includes small molecules and biologics.

YTD Price Performance: -19.77%

Average Trading Volume: 6,299

Technical Sentiment Signal: Buy

Current Market Cap: $547.1M

Learn more about PHAR stock on TipRanks’ Stock Analysis page.

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